Pubblicazioni

CRISPR/Cas9–mediated deletion of CTG expansions recovers normal phenotype in myogenic cells derived from myotonic dystrophy 1 patients

2017 - MOLECULAR THERAPY NUCLEIC ACIDS
Provenzano, Claudia; Cappella, Marisa; Valaperta, Rea; Cardani, Rosanna; Meola, Giovanni; Martelli, Fabio; Cardinali, Beatrice; Falcone, Germana

© Università degli Studi di Roma "La Sapienza" - Piazzale Aldo Moro 5, 00185 Roma