Pubblicazioni

Human iPSC model reveals a central role for NOX4 and oxidative stress in Duchenne cardiomyopathy

2022 - STEM CELL REPORTS

Duelen, R.; Costamagna, D.; Gilbert, G.; Waele, L. D.; Goemans, N.; Desloovere, K.; Verfaillie, C. M.; Sipido, K. R.; Buyse, G. M.; Sampaolesi, M.

Time-controlled and muscle-specific CRISPR/Cas9-mediated deletion of CTG-repeat expansion in the DMPK gene

2022 - MOLECULAR THERAPY NUCLEIC ACIDS

Cardinali, B.; Provenzano, C.; Izzo, M.; Voellenkle, C.; Battistini, J.; Strimpakos, G.; Golini, E.; Mandillo, S.; Scavizzi, F.; Raspa, M.; Perfetti, A.; Baci, D.; Lazarevic, D.; Garcia-Manteiga, J. M.; Gourdon, G.; Martelli, F.; Falcone, G.

Molecular Therapies for Myotonic Dystrophy Type 1: From Small Drugs to Gene Editing

2022 - INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES

Izzo, Mariapaola; Battistini, Jonathan Isacco; Provenzano, Claudia; Martelli, Fabio; Cardinali, Beatrice; Falcone, Germana