Pubblicazioni

Revolutionizing CAR T-Cell Therapies: Innovations in Genetic Engineering and Manufacturing to Enhance Efficacy and Accessibility

2024 - INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES

Giorgioni, Lorenzo; Ambrosone, Alessandra; Cometa, Maria Francesca Paola; Salvati, Anna Laura; NisticÃ², Robert; Magrelli, Armando

Unveiling the Future of Cardiac Care: A Review of Gene Therapy in Cardiomyopathies

2024 - INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES

Venturiello, Damiano; Tiberi, Pier Giorgio; Perulli, Francesco; Nardoianni, Giulia; Guida, Leonardo; Barsali, Carlo; Terrone, Carlo; Cianca, Alessandro; Lustri, Camilla; Sclafani, Matteo; Tini, Giacomo; Barbato, Emanuele; Musumeci, Beatrice

Nano-immunomodulation: a new strategy for skeletal muscle diseases and aging?

2023 - INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES

Millozzi, Francesco; Papait, Andrea; Bouche', Marina; Parolini, Ornella; Palacios, Daniela

CRISPR/Cas9 and piggyBac Transposon-Based Conversion of a Pathogenic Biallelic TBCD Variant in a Patient-Derived iPSC Line Allows Correction of PEBAT-Related Endophenotypes

2023 - INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES

Muto, Valentina; Benigni, Federica; Magliocca, Valentina; Borghi, Rossella; Flex, Elisabetta; Pallottini, Valentina; Rosa, Alessandro; Compagnucci, Claudia; Tartaglia, Marco

Molecular Therapies for Myotonic Dystrophy Type 1: From Small Drugs to Gene Editing

2022 - INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES

Izzo, Mariapaola; Battistini, Jonathan Isacco; Provenzano, Claudia; Martelli, Fabio; Cardinali, Beatrice; Falcone, Germana